Harmatz, PR; Whitley, C; Steiner, R; Plecko, B; Kaplan, P; Waterson, J; Ketteridge, D; Giugliani, R; Schwartz, I; Guffon, N; Miranda, CS; Keppen, L; Teles, E; Hopwood, J.
Update on phase I/II and phase II studies of recombinant human N-acetylgalactosamine 4-sulfatase (rhASB)) enzyme replacement therapy in patients with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome).
GENET MED 2004 6: 248-248.
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